Posts

Sensorion advances hearing loss gene therapy programs

Servier inks up to $2.65B buyout of Edgewise's muscular dystrophy unit to boost neurology pipeline

After Tumultuous Year, Sarepta Plots Rebound with Early Data on RNA Therapies

Entrada tightens focus on Duchenne, axes 20% of staff

Biotech Restructuring and European Regulatory Setbacks

Wave Life Sciences' WVE-N531 Shows Promise in Duchenne Muscular Dystrophy Treatment

Epicrispr raises $68M, will start clinical trial of epigenetic editing for FSHD

Sarepta Reports Death of DMD Patient Following Elevidys Gene Therapy Treatment

Avidity's Del-zota Shows Promise in Duchenne Muscular Dystrophy Treatment

Entrada given go-ahead to test DMD therapy after two-year hold

FDA Lifts Clinical Hold on Entrada's Duchenne Muscular Dystrophy Drug ENTR-601-44 After Two Years

Solid Biosciences' DMD Gene Therapy Shows Promising Early Results, Driving Stock Surge

Sarepta Therapeutics Reports Encouraging Two-Year Data for ELEVIDYS in Duchenne Muscular Dystrophy, Projecting $1 Billion in Sales