Posts

Rare Disease Sales Projected to Exceed $400B by 2032 Despite Challenges, Driven by Small Molecule Resurgence

FDA Accelerates Rare Disease Drug Approvals with New Frameworks and Record 2025 Approvals

US Spending Bill Tweaks Orphan Drug Exclusion to Broaden Protections and Ease FDA Burden

Spotlight On: AI in Genomics and Multimodal Data Analysis Loosens Orphan Drug R&D Bottlenecks

Orphan Drug Trends: A Data-Driven Analysis

Spotlight On: Five Key FDA Approvals of 2025

Unlocking Japan's Potential in Rare Disease Drug Development: Recent Progress and Challenges (2025)

FDA Grants Dupixent (Dupilumab) Eighth Approval: Now Cleared for Bullous Pemphigoid

Regeneron Leads $66M Series B for Actio Biosciences’ Rare Disease Therapeutics

Senate Drops Orphan Cures Act from Trump's Tax Bill, Dealing Setback to Biopharma