FDA Investigates Patient Deaths Linked to Sarepta's Elevidys Gene Therapy for Duchenne Muscular Dystrophy on June 25, 2025 Elevidys Evaluation gene therapy Liver Liver Failure, Acute Muscular Dystrophy, Duchenne patient deaths regulatory Toxicity aspects Unable to walk (finding) United States Food and Drug Administration +
Second Patient Dies After Receiving Sarepta's Elevidys Gene Therapy for DMD on June 17, 2025 AAV-based gene therapy Elevidys gene therapy Liver Failure, Acute Muscular Dystrophy, Duchenne Patient Death risk mitigation Unable to walk (finding) United States Food and Drug Administration +
Sarepta Halts Duchenne Gene Therapy in Some Patients After Second Death on June 16, 2025 Clinical Trials Elevidys gene therapy Liver Failure, Acute Muscular Dystrophy, Duchenne patient safety Therapeutic immunosuppression Unable to walk (finding) United States Food and Drug Administration +