FDA Approves Leucovorin for Rare Cerebral Folate Deficiency Without New Trial Data on March 11, 2026 Approved CFD-FOLR1 Clinical Trials Evidence leucovorin Neurodegeneration Due To Cerebral Folate Transport Deficiency real-world United States Food and Drug Administration Wellcovorin +
FDA's Move to Update GSK's Leucovorin for Autism Raises Questions on Dose, Supply, and Data on September 24, 2025 Autistic Disorder Clinical Data Dosage drug relabeling leucovorin Neurodegeneration Due To Cerebral Folate Transport Deficiency SmithKline Beecham United States Food and Drug Administration Wellcovorin +